About | Contact | Sitemap | Home   

Search:     

    


About Us

MPS & Related Diseases

Treatments & Clinical Trials

News & Events

Membership

Family Support

Library

Research Grants

Pharmaceutical Partners

Legislative

Fundraisers

Walk/Run

Donate

Press Room

Tributes

Home

Gallery

MPS Logo Shop



News & Events > National MPS Society News

National MPS Society News

Dr. Emil Kakkis and Dr. Jenny Soriano complete $1 million pledge

In 2006, Drs. Emil Kakkis and Jenny Soriano pledged $1 million dollars to the National MPS Society’s Endowment Fund.  This generous donation was scheduled to be given over five years.   We are honored to report that Drs. Kakkis and Soriano completed their pledge in December 2009, one year earlier than scheduled. 

Emil Kakkis, MD, PhD began his work at Harbor-UCLA to develop novel treatments for neglected rare disorders and developed the enzyme replacement therapy for MPS I, Aldurazyme.  Aldurazyme development was later supported by BioMarin™ and eventually their partner Genzyme™ leading to FDA approval in 2003.

During his tenure at BioMarin, Dr. Kakkis guided the development and approval of two more treatments for rare disorders, MPS VI and PKU and has contributed to the initiation of seven other treatment programs for rare disorders, three of which are now in clinical development. Dr. Kakkis has left his position as Chief Medical Officer of BioMarin to pursue changes in the drug development and regulatory system. His focus is now on improving the diagnosis and treatment of rare disorders; specifically the process by which treatments for rare disorders are tested and approved, through the Kakkis EveryLife Foundation.

Dr. Kakkis received the Lifetime Achievement Award from the National MPS Society for his work on Aldurazyme.

The National MPS Society’s Endowment Fund is a permanent endowment, the earnings from which are used to support the Society’s administrative operations in perpetuity.


 National MPS Society Communications Survey Results

The results are in for the National MPS Society Communcations survey! More...





About Us | MPS & Related Diseases | Treatments & Clinical Trials | News & Events | Membership | Family Support
Library | Research Grants | Pharmaceutical Partners | Legislative | Fundraisers | Walk/Run
Donate | Press Room | Tributes | Home | Gallery | MPS Logo Shop

© 2005 - 2010 National MPS Society. All Rights Reserved Site developed and hosted by sephone internet solutions.